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A Designer AAV Variant Permits Efficient Retrograde Access to Projection Neurons
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Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo
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Efficient generation of targeted large insertions by microinjection into two-cell-stage mouse embryos
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Nature biotechnology, 2018, Vol.36 (7), p.632-637
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A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice
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Nature biotechnology, 2016, Vol.34 (3), p.334-338
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Therapeutic Applications of Extracellular Vesicles: Clinical Promise and Open Questions
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Exosomes from marrow stromal cells expressing miR-146b inhibit glioma growth
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Adoptive Immunotherapy for Cancer or Viruses
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