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by Alterman, Julia F
Nature biotechnology, 2019-08, Vol.37 (8), p.884-894

2.
Artificial miRNAs Reduce Human Mutant Huntingtin Throughout the Striatum in a Transgenic Sheep Model of Huntington's Disease
by Pfister, Edith L.
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3.
Full sequence of mutant huntingtin 3'-untranslated region and modulation of its gene regulatory activity by endogenous microRNA
by Kim, Kyung-Hee
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4.
Dose-Dependent Lowering of Mutant Huntingtin Using Antisense Oligonucleotides in Huntington Disease Patients
by Willeke MC van Roon-Mom
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5.
Mutated Huntingtin Causes Testicular Pathology in Transgenic Minipig Boars
by Macakova, Monika
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6.
The Biology of Huntingtin
by Saudou, Frédéric
Neuron (Cambridge, Mass.), 2016-03-02, Vol.89 (5), p.910-926

7.
Mutant Huntingtin Disrupts the Nuclear Pore Complex
by Grima, Jonathan C
Neuron (Cambridge, Mass.), 2017-04-05, Vol.94 (1), p.93-107.e6

8.
Polyglutamine-Expanded Huntingtin Exacerbates Age-Related Disruption of Nuclear Integrity and Nucleocytoplasmic Transport
by Gasset-Rosa, Fatima
Neuron (Cambridge, Mass.), 2017-04-05, Vol.94 (1), p.48-57.e4

9.
Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington's disease
by Zeitler, Bryan
Nature medicine, 2019-07, Vol.25 (7), p.1131-1142

10.
Mutant huntingtin binds the mitochondrial fission GTPase dynamin-related protein-1 and increases its enzymatic activity
by Petrilli, Alejandra
Nature medicine, 2011-03, Vol.17 (3), p.377-382

11.
RAN Translation in Huntington Disease
by Bañez-Coronel, Monica
Neuron (Cambridge, Mass.), 2015-11-18, Vol.88 (4), p.667-677

12.
Balance between synaptic versus extrasynaptic NMDA receptor activity influences inclusions and neurotoxicity of mutant huntingtin
by Talantova, Maria
Nature medicine, 2009-12, Vol.15 (12), p.1407-1413

13.
Sustained Therapeutic Reversal of Huntington's Disease by Transient Repression of Huntingtin Synthesis
by Kordasiewicz, Holly B
Neuron (Cambridge, Mass.), 2012-06-21, Vol.74 (6), p.1031-1044

14.
The roles of intracellular protein-degradation pathways in neurodegeneration
by Rubinsztein, David C
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15.
Sirt1 mediates neuroprotection from mutant huntingtin by activation of the TORC1 and CREB transcriptional pathway
by Jeong, Hyunkyung
Nature medicine, 2011-12-18, Vol.18 (1), p.159-165

16.
Network Organization of the Huntingtin Proteomic Interactome in Mammalian Brain
by Shirasaki, Dyna I
Neuron (Cambridge, Mass.), 2012-07-12, Vol.75 (1), p.41-57

17.
Neuroprotective role of Sirt1 in mammalian models of Huntington's disease through activation of multiple Sirt1 targets
by Jiang, Mali
Nature medicine, 2011-12-18, Vol.18 (1), p.153-158

18.
Physico-Pathologic Mechanisms Involved in Neurodegeneration: Misfolded Protein-Plasma Membrane Interactions
by Shrivastava, Amulya Nidhi
Neuron (Cambridge, Mass.), 2017-07-05, Vol.95 (1), p.33-50

19.
Huntingtin-Mediated Multipolar-Bipolar Transition of Newborn Cortical Neurons Is Critical for Their Postnatal Neuronal Morphology
by Barnat, Monia
Neuron (Cambridge, Mass.), 2017-01-04, Vol.93 (1), p.99-114

20.
Inhibitors of protein disulfide isomerase suppress apoptosis induced by misfolded proteins
by Stockwell, Brent R
Nature chemical biology, 2010-12, Vol.6 (12), p.900-906
