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Nature biotechnology, 2006-03, Vol.24 (2), p.198-204

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Gene Delivery Improvement for Treating the Lysosomal Storage Disorder Metachromatic Leukodystrophy
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MHC class I protects motor neurons from astrocyte-induced toxicity in amyotrophic lateral sclerosis (ALS)
by Song, SungWon SungWon
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by Cheever, Thomas R.
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by Frakes, Ashley E
Neuron (Cambridge, Mass.), 2014-03-05, Vol.81 (5), p.1009

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Intravascular AAV9 preferentially targets neonatal-neurons and adult-astrocytes in CNS
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Nature biotechnology, 2008-12-21, Vol.27 (1), p.59-65

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Spinal subpial delivery of AAV9 enables widespread gene silencing and blocks motoneuron degeneration in ALS
by Bravo-Hernandez, Mariana
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Could gene therapy be the future for muscular dystrophy?
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Astrocytes from familial and sporadic ALS patients are toxic to motor neurons
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