1.
Genome editing in mitochondria corrects a pathogenic mtDNA mutation in vivo
by Gammage, Payam A
Nature medicine, 2018, Vol.24 (11), p.1691-1695

2.
Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington's disease
by Zeitler, Bryan
Nature medicine, 2019, Vol.25 (7), p.1131-1142
